![Intrinsically cell-penetrating multivalent and multitargeting ligands for myotonic dystrophy type 1 | PNAS Intrinsically cell-penetrating multivalent and multitargeting ligands for myotonic dystrophy type 1 | PNAS](https://www.pnas.org/cms/10.1073/pnas.1820827116/asset/d98dfffd-fd04-4773-9168-d4b94d410391/assets/graphic/pnas.1820827116fig01.jpeg)
Intrinsically cell-penetrating multivalent and multitargeting ligands for myotonic dystrophy type 1 | PNAS
![Genetics of Myotonic Dystrophy (MD) and Fascioscapulohumeral Dystrophy (FSHD) - Educational Resources - National Registry for Myotonic Dystrophy (DM) and Facioscapulohumeral Dystrophy (FSHD) - Neurology - University of Rochester Medical Center Genetics of Myotonic Dystrophy (MD) and Fascioscapulohumeral Dystrophy (FSHD) - Educational Resources - National Registry for Myotonic Dystrophy (DM) and Facioscapulohumeral Dystrophy (FSHD) - Neurology - University of Rochester Medical Center](https://www.urmc.rochester.edu/MediaLibraries/URMCMedia/neurology/images/image002.gif)
Genetics of Myotonic Dystrophy (MD) and Fascioscapulohumeral Dystrophy (FSHD) - Educational Resources - National Registry for Myotonic Dystrophy (DM) and Facioscapulohumeral Dystrophy (FSHD) - Neurology - University of Rochester Medical Center
![Model for the molecular consequences of triplet expansion in DM1. In... | Download Scientific Diagram Model for the molecular consequences of triplet expansion in DM1. In... | Download Scientific Diagram](https://www.researchgate.net/publication/45094641/figure/fig3/AS:753004605104128@1556541696465/Model-for-the-molecular-consequences-of-triplet-expansion-in-DM1-In-healthy-subjects.jpg)
Model for the molecular consequences of triplet expansion in DM1. In... | Download Scientific Diagram
![Genome Editing of Expanded CTG Repeats within the Human DMPK Gene Reduces Nuclear RNA Foci in the Muscle of DM1 Mice: Molecular Therapy Genome Editing of Expanded CTG Repeats within the Human DMPK Gene Reduces Nuclear RNA Foci in the Muscle of DM1 Mice: Molecular Therapy](https://www.cell.com/cms/attachment/db288fe8-ec35-4ef3-9ea5-6b54d0680140/gr1_lrg.jpg)
Genome Editing of Expanded CTG Repeats within the Human DMPK Gene Reduces Nuclear RNA Foci in the Muscle of DM1 Mice: Molecular Therapy
![Time-controlled and muscle-specific CRISPR/Cas9-mediated deletion of CTG-repeat expansion in the DMPK gene: Molecular Therapy - Nucleic Acids Time-controlled and muscle-specific CRISPR/Cas9-mediated deletion of CTG-repeat expansion in the DMPK gene: Molecular Therapy - Nucleic Acids](https://www.cell.com/cms/asset/4eaf969c-41b7-4f28-ae40-95febd68e6e8/fx1.jpg)
Time-controlled and muscle-specific CRISPR/Cas9-mediated deletion of CTG-repeat expansion in the DMPK gene: Molecular Therapy - Nucleic Acids
![RNA toxic gain-of-function model for DM1 pathogenesis. Mutant DMPK RNA... | Download Scientific Diagram RNA toxic gain-of-function model for DM1 pathogenesis. Mutant DMPK RNA... | Download Scientific Diagram](https://www.researchgate.net/publication/331135954/figure/fig2/AS:727691837833217@1550506662044/RNA-toxic-gain-of-function-model-for-DM1-pathogenesis-Mutant-DMPK-RNA-accumulates-in-the.jpg)
RNA toxic gain-of-function model for DM1 pathogenesis. Mutant DMPK RNA... | Download Scientific Diagram
![IJMS | Free Full-Text | Molecular Therapies for Myotonic Dystrophy Type 1: From Small Drugs to Gene Editing IJMS | Free Full-Text | Molecular Therapies for Myotonic Dystrophy Type 1: From Small Drugs to Gene Editing](https://www.mdpi.com/ijms/ijms-23-04622/article_deploy/html/images/ijms-23-04622-g001.png)
IJMS | Free Full-Text | Molecular Therapies for Myotonic Dystrophy Type 1: From Small Drugs to Gene Editing
![Myotonic Dystrophy Type 2: An Update on Clinical Aspects, Genetic and Pathomolecular Mechanism | Semantic Scholar Myotonic Dystrophy Type 2: An Update on Clinical Aspects, Genetic and Pathomolecular Mechanism | Semantic Scholar](https://d3i71xaburhd42.cloudfront.net/d1cef90e69961480ac8901cf04d4d320989a6103/5-Figure2-1.png)
Myotonic Dystrophy Type 2: An Update on Clinical Aspects, Genetic and Pathomolecular Mechanism | Semantic Scholar
![Application of CRISPR-Cas9-Mediated Genome Editing for the Treatment of Myotonic Dystrophy Type 1: Molecular Therapy Application of CRISPR-Cas9-Mediated Genome Editing for the Treatment of Myotonic Dystrophy Type 1: Molecular Therapy](https://www.cell.com/cms/attachment/1ab7b752-b62a-4f51-888b-dc27651f833d/fx1_lrg.jpg)
Application of CRISPR-Cas9-Mediated Genome Editing for the Treatment of Myotonic Dystrophy Type 1: Molecular Therapy
![Developmental insights into the pathology of and therapeutic strategies for DM1: Back to the basics - Chau - 2015 - Developmental Dynamics - Wiley Online Library Developmental insights into the pathology of and therapeutic strategies for DM1: Back to the basics - Chau - 2015 - Developmental Dynamics - Wiley Online Library](https://anatomypubs.onlinelibrary.wiley.com/cms/asset/a73e6464-578e-4406-9e1c-a35dfb2d5ebc/dvdy24240-fig-0001-m.jpg)
Developmental insights into the pathology of and therapeutic strategies for DM1: Back to the basics - Chau - 2015 - Developmental Dynamics - Wiley Online Library
DM1 pathogenetic mechanisms and therapeutic strategies. The actions of... | Download Scientific Diagram
![Additional molecular pathogenetic mechanisms in DM1. Results suggest an... | Download Scientific Diagram Additional molecular pathogenetic mechanisms in DM1. Results suggest an... | Download Scientific Diagram](https://www.researchgate.net/publication/255957983/figure/fig4/AS:267570947293196@1440805293206/Additional-molecular-pathogenetic-mechanisms-in-DM1-Results-suggest-an-additional.png)